regulatory pathway for drugs
Rare Disease Day: What is a Rare Disease and What are Orphan Drugs?
- February 26, 2019
- Posted by: AXSource
- Category: Blog, Regulatory and Quality
What is a Rare Disease? A rare disease is a life-threatening, seriously debilitating or chronic condition affecting a fairly small number of patients. A disease may be considered rare in one part of the world, or in a particular group of people, but still be common in another. For instance, in the United States the